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Global Open-Label Extension Study of Del-desiran for the Treatment of DM1 | Clinical Trials | Clareo Health

Enrolling By InvitationPhase 3NCT07008469

Global Open-Label Extension Study of Del-desiran for the Treatment of DM1

A Global Phase 3 Open-Label Extension Study to Assess the Long-Term Safety, Tolerability, and Efficacy of Intravenous Delpacibart Etedesiran (abbreviated del-desiran, formerly AOC 1001) for the Treatm...

Lead sponsor: Avidity Biosciences, Inc.•17 U.S. locations•View source on ClinicalTrials.gov

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Data from ClinicalTrials.govLast updated on ClinicalTrials.gov: April 23, 2026Terms

Trial snapshot

StatusENROLLING_BY_INVITATION

PhasePHASE3

Enrollment230

Start dateJul 2025

Last updatedApr 23, 2026

Condition

Myotonic Dystrophy Type 1 DM1 Myotonic Dystrophy Myotonia Myotonic Dystrophy 1+3 more

Locations shown

University of California, Los Angeles (UCLA)

Los Angeles, California

Stanford University

Stanford, California

University of Colorado

Denver, Colorado

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Data Source & Attribution

This clinical trial information is sourced from ClinicalTrials.gov, a service of the U.S. National Institutes of Health.

ClinicalTrials.gov last update: April 23, 2026Data synced to Clareo: May 10, 2026

Modifications: This data has been reformatted for display purposes. Eligibility criteria have been parsed into inclusion/exclusion sections. Location data has been geocoded to enable distance-based search. For the authoritative and most current information, please visit ClinicalTrials.gov.

Neither the United States Government nor Clareo Health make any warranties regarding the data. Check ClinicalTrials.gov frequently for updates.

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