Finding studies
Finding studies
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Ionis Pharmaceuticals, Inc.
CONTACT
Lead
Ionis Pharmaceuticals, Inc.
This is an open-label study of ION337 in people with DS between the ages of 2 and 12 years old (inclusive). The study consists of 2 parts: Part 1) 6-month single ascending dose (SAD) and Part 2) 24-month multiple ascending dose (MAD), followed by a 7-month safety follow up.
Age
2–12
Sex
ALL
Healthy volunteers
Not accepted