Finding studies
Finding studies
Take this into the appointment.
Saves the questions and what to expect into your notes, next to the visit they belong to.
Broad Institute
CONTACT
Lead
Broad Institute of MIT and Harvard
With
This is a first-in-human, open label, single ascending dose study. The study will consist of a screening period of up to 2 weeks, administration of a single intrathecal dose of PrP-siRNA, and a 24-week follow-up period. Multiple dose levels will be tested. This trial also includes an observational arm in which symptomatic participants will not receive investigational drug, and will be followed for an 8-week period after baseline.
Age
18–any
Sex
ALL
Healthy volunteers
Not accepted