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A Phase 2, Randomized, Double-Blind, Placebo-Controlled, Multicenter Study to Evaluate the Safety and Efficacy of Vosoritide in Infants and Young Children With Hypochondroplasia, Aged 0 to < 36 Months
Conditions
Interventions
Vosoritide
Placebo
Locations
26
United States
Phoenix Children's Hospital - Thomas Campus (Main)
Phoenix, Arizona, United States
Cedars-Sinai Medical Center
Los Angeles, California, United States
Benioff Children's Hospital - Oakland
Oakland, California, United States
Children's National Medical Center
Washington D.C., District of Columbia, United States
Ann & Robert H. Lurie Children's Hospital of Chicago
Chicago, Illinois, United States
The Johns Hopkins University School of Medicine
Baltimore, Maryland, United States
Start Date
July 30, 2025
Primary Completion Date
June 30, 2028
Completion Date
June 30, 2028
Last Updated
March 31, 2026
NCT06212947
NCT06873035
NCT06455059
Lead Sponsor
BioMarin Pharmaceutical
Collaborators
Data Source & Attribution
This clinical trial information is sourced from ClinicalTrials.gov, a service of the U.S. National Institutes of Health.
Modifications: This data has been reformatted for display purposes. Eligibility criteria have been parsed into inclusion/exclusion sections. Location data has been geocoded to enable distance-based search. For the authoritative and most current information, please visit ClinicalTrials.gov.
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