Expanded Access Study of UC-MSC in DMD Patients

Inclusion Criteria

• •1. Male sex by birth with a genetically confirmed diagnosis of Duchenne Muscular Dystrophy (DMD).
• •2. Age is greater than or equal to 5 and less than or equal to 10 years.
• •3. Has a North Star Ambulatory Assessment (NSAA) score greater than 13 and less than 30.
• •4. Demonstrates the ability to perform the "time to rise" test in under 10 seconds.
• •5. Is up-to-date on immunizations.
• •6. Is on a stable dose of glucocorticoids for at least 12 weeks prior to study participation, except for weight-based or toxicity-related adjustments.
• •7. Is on a stable dose of supplements for at least 12 weeks prior to study participation.
• •8. Has the ability to comply with the requirements of the study and the ability to understand and provide written informed assent and a guardian's consent.
• •9. Patient must be either a non-responder to or a poor candidate for treatment with another established therapy.