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Prospective Longitudinal Study of Neurological Disease Trajectory in Children Living With Late-Infantile or Juvenile Onset of GM1 or GM2 Gangliosidosis
Conditions
Locations
13
United States
UCSF Benioff Children's Hospital
Oakland, California, United States
Mayo Clinic Rochester
Rochester, Minnesota, United States
Hospital Pequeno Principe
Curitiba, Brazil
Hospital de Clinicas de Porto Alegre
Porto Alegre, Brazil
Hopital d'Enfants CHU Timone
Marseille, France
Armand-Trousseau Children's Hospital - CHU Paris Est
Paris, France
Start Date
February 22, 2022
Primary Completion Date
September 16, 2025
Completion Date
September 16, 2025
Last Updated
September 29, 2025
NCT03333200
NCT02254863
NCT06614569
NCT04713475
NCT07479953
NCT04669535
Lead Sponsor
Azafaros A.G.
Data Source & Attribution
This clinical trial information is sourced from ClinicalTrials.gov, a service of the U.S. National Institutes of Health.
Modifications: This data has been reformatted for display purposes. Eligibility criteria have been parsed into inclusion/exclusion sections. Location data has been geocoded to enable distance-based search. For the authoritative and most current information, please visit ClinicalTrials.gov.
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