Loading clinical trials...

A Safety and Efficacy Study Evaluating ET-01 in Subjects with Transfusion Dependent Β-Thalassaemia | Clinical Trials | Clareo Health

Back to clinical trial search

TERMINATEDPhase 1NCT04925206

A Safety and Efficacy Study Evaluating ET-01 in Subjects with Transfusion Dependent Β-Thalassaemia

This is a single-arm, open label, multi-center, single-dose phase 1 study in subjects with transfusion dependent β-thalassaemia. The study will evaluate the safety and efficacy of autologous CRISPR-Ca...

Lead sponsor: EdiGene (GuangZhou) Inc.•4 locations•View source on ClinicalTrials.gov

Clareo plain-language summary

What this study is about

Generating AI summary...

Save this trial guide to your notes

Keep your clinical trial research organized — questions to ask, what to expect, and key details.

Related studies

RECRUITINGPhase 1

Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies

NCT06647979 · Sickle Cell Disease, Sickle Cell Anemia (HbSS, or HbSβ-thalassemia0), and more

Data from ClinicalTrials.govLast updated on ClinicalTrials.gov: March 30, 2025Terms

Trial snapshot

StatusTERMINATED

PhasePHASE1

Enrollment8

Start dateAug 2021

Last updatedMar 30, 2025

Condition

Transfusion Dependent Beta-Thalassaemia

Locations shown

Nanfang Hospital of Southern Medical University

Guangzhou, Guangdong

Guangzhou Women and Children's Medical Center

Guangzhou, Guangdong

Shenzhen Children's Hospital

Shenzhen, Guangdong

For caregivers

Use Clareo to keep notes, questions, trial details, and next steps organized before and after appointments.

Start free trial →

Data Source & Attribution

This clinical trial information is sourced from ClinicalTrials.gov, a service of the U.S. National Institutes of Health.

ClinicalTrials.gov last update: March 30, 2025Data synced to Clareo: May 25, 2026

Modifications: This data has been reformatted for display purposes. Eligibility criteria have been parsed into inclusion/exclusion sections. Location data has been geocoded to enable distance-based search. For the authoritative and most current information, please visit ClinicalTrials.gov.

Neither the United States Government nor Clareo Health make any warranties regarding the data. Check ClinicalTrials.gov frequently for updates.

View ClinicalTrials.gov Terms and Conditions