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A Pilot, Open-label, Single Arm, Multicenter Study to Evaluate Safety, Tolerability, Pharmacokinetics and Efficacy of Intravenous Administrations of Emapalumab, an Anti-interferon Gamma (Anti-IFNγ) Monoclonal Antibody, in Patients With Systemic Juvenile Idiopathic Arthritis (sJIA) or Adult-onset Still's Disease (AOSD) Developing Macrophage Activation Syndrome/Secondary HLH (MAS/sHLH)
Conditions
Interventions
Emapalumab
Locations
5
United States
Cincinnati Children'S Hospital
Cincinnati, Ohio, United States
Hôpital Necker-Enfants Malades, Unité d'Immunologie-hématologie et Rhumatologie pédiatriques
Paris, France
IRCCS Ospedale Pediatrico, Bambino Gesù
Rome, Italy
Hospital Sant Joan de Deu
Barcelona, Spain
Great Ormond Street Hospital for Children
London, United Kingdom
Start Date
February 20, 2018
Primary Completion Date
May 19, 2020
Completion Date
May 19, 2020
Last Updated
May 17, 2022
NCT07339345
NCT06383195
NCT07349667
NCT06718569
NCT03332225
NCT00868751
Lead Sponsor
Swedish Orphan Biovitrum
Data Source & Attribution
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