Saves the questions and what to expect into your notes, next to the visit they belong to.
Keep this study
Lead
Ra Pharmaceuticals
Age
18–any
Sex
ALL
Healthy volunteers
Not accepted
You may be eligible if
Diagnosis of PNH by flow cytometry
Inadequate response to eculizumab defined as having received eculizumab for at least 6 months plus a documented LDH level ≥ 1.5 x the upper limit of normal (ULN) and/or the presence of a known C5 mutation conferring resistance to eculizumab
You may not be if
History of meningococcal disease
Current systemic infection or suspicion of active bacterial infection
