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A Phase 3 Single Arm Study Evaluating the Efficacy and Safety of Gene Therapy in Subjects With Transfusion-dependent β-Thalassemia, Who do Not Have a β0/β0 Genotype, by Transplantation of Autologous CD34+ Stem Cells Transduced Ex Vivo With a Lentiviral βA-T87Q-Globin Vector in Subjects ≤50 Years of Age
Conditions
Interventions
LentiGlobin BB305 Drug Product
Locations
8
United States
Oakland, California, United States
Chicago, Illinois, United States
Philadelphia, Pennsylvania, United States
Marseille, France
Hanover, Germany
Rome, Italy
Start Date
August 8, 2016
Primary Completion Date
March 31, 2022
Completion Date
March 31, 2022
Last Updated
June 18, 2023
NCT06647979
NCT06308159
NCT03653338
NCT06772766
NCT06606886
NCT05762510
Lead Sponsor
Genetix Biotherapeutics Inc.
Data Source & Attribution
This clinical trial information is sourced from ClinicalTrials.gov, a service of the U.S. National Institutes of Health.
Modifications: This data has been reformatted for display purposes. Eligibility criteria have been parsed into inclusion/exclusion sections. Location data has been geocoded to enable distance-based search. For the authoritative and most current information, please visit ClinicalTrials.gov.
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