Saves the questions and what to expect into your notes, next to the visit they belong to.
Keep this study
Lead
StemCells, Inc.
Participation in this study will involve screening assessments, surgery to implant HuCNS-SC, medication to suppress immune system and a series of follow-up assessments.
Age
0–6
Sex
ALL
Healthy volunteers
Not accepted
You may be eligible if
Age 6 months to 6 years
Male or female
Clinical diagnosis of Infantile neuronal ceroid lipofuscinosis or late infantile neuronal ceroid lipofuscinosis
CLN1 or CLN2 mutation
You may not be if
Previously received an organ, tissue or bone marrow transplantation
Previously participated in any gene or cell therapy study
Infection with hepatitis virus, cytomegalovirus, Epstein-Barr virus, or Human Immunodeficiency Virus (HIV)
Current or prior cancer
Bleeding disorder
Unable to have an MRI scan
Clareo Health | Safety and Efficacy Study of HuCNS-SC in Subjects With Neuronal Ceroid Lipofuscinosis
