Question 1

What specific benefits can I expect from continuing Myozyme treatment?

Accepted Answer

This is a question you may want to discuss with your doctor regarding the Extension Study of Patients With Infantile-Onset Pompe Disease Who Were Previously Enrolled in Protocol AGLU01602 clinical trial (NCT00125879). Contact the study team or your healthcare provider for specific answers.

Question 2

Are there any new side effects I should be aware of with long-term use?

Accepted Answer

This is a question you may want to discuss with your doctor regarding the Extension Study of Patients With Infantile-Onset Pompe Disease Who Were Previously Enrolled in Protocol AGLU01602 clinical trial (NCT00125879). Contact the study team or your healthcare provider for specific answers.

Question 3

How will my progress be monitored during this study?

Accepted Answer

This is a question you may want to discuss with your doctor regarding the Extension Study of Patients With Infantile-Onset Pompe Disease Who Were Previously Enrolled in Protocol AGLU01602 clinical trial (NCT00125879). Contact the study team or your healthcare provider for specific answers.

Question 4

What happens if I experience side effects while participating?

Accepted Answer

This is a question you may want to discuss with your doctor regarding the Extension Study of Patients With Infantile-Onset Pompe Disease Who Were Previously Enrolled in Protocol AGLU01602 clinical trial (NCT00125879). Contact the study team or your healthcare provider for specific answers.

Question 5

How does this study fit with other treatment options available for my condition?

Accepted Answer

This is a question you may want to discuss with your doctor regarding the Extension Study of Patients With Infantile-Onset Pompe Disease Who Were Previously Enrolled in Protocol AGLU01602 clinical trial (NCT00125879). Contact the study team or your healthcare provider for specific answers.

What this study is about