Question 1

What specific long-term effects should I expect to be monitored in this study?

Accepted Answer

This is a question you may want to discuss with your doctor regarding the Long-term Follow-up of Subjects With Transfusion-Dependent β-Thalassemia (TDT) Treated With Ex Vivo Gene Therapy clinical trial (NCT02633943). Contact the study team or your healthcare provider for specific answers.

Question 2

How will the findings from this follow-up study impact my future treatment options?

Accepted Answer

This is a question you may want to discuss with your doctor regarding the Long-term Follow-up of Subjects With Transfusion-Dependent β-Thalassemia (TDT) Treated With Ex Vivo Gene Therapy clinical trial (NCT02633943). Contact the study team or your healthcare provider for specific answers.

Question 3

Are there any risks associated with participating in this long-term follow-up?

Accepted Answer

This is a question you may want to discuss with your doctor regarding the Long-term Follow-up of Subjects With Transfusion-Dependent β-Thalassemia (TDT) Treated With Ex Vivo Gene Therapy clinical trial (NCT02633943). Contact the study team or your healthcare provider for specific answers.

Question 4

What kind of assessments will be done during the follow-up period?

Accepted Answer

This is a question you may want to discuss with your doctor regarding the Long-term Follow-up of Subjects With Transfusion-Dependent β-Thalassemia (TDT) Treated With Ex Vivo Gene Therapy clinical trial (NCT02633943). Contact the study team or your healthcare provider for specific answers.

Question 5

How often will I need to visit for assessments during this study?

Accepted Answer

This is a question you may want to discuss with your doctor regarding the Long-term Follow-up of Subjects With Transfusion-Dependent β-Thalassemia (TDT) Treated With Ex Vivo Gene Therapy clinical trial (NCT02633943). Contact the study team or your healthcare provider for specific answers.

What this study is about