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CPAP for Infantile Pompe Disease | Clinical Trials | Clareo Health

UNKNOWNPHASE4

CPAP for Infantile Pompe Disease

Efficacy of Continuous Positive Airway Pressure of Treatment of Hypernasality of Children With Infantile Pompe Disease

NCT02405624•National Taiwan University Hospital

Summary

Patients with infantile onset Pompe disease will be trained with continuous positive airway pressure to see if hypernasality can be improved.

Eligibility

Age

4 - No limit years

Sex

ALL

Healthy Volunteers

Yes

Inclusion Criteria

•1. confirm as Pompe disease
•2. Age 4 and can speak 2-words sentence by order
•3. mild to severe hypernasality
•4. have regular speech therapy for 8 weeks or longer

Exclusion Criteria

•(1）hearing loss （2）congenital pharyngeal or laryngeal structure anomalies including cleft palate （3）cerebral palsy （4）recent otitis media effusion （5）very severe hypernasality （6）use non-invasive ventilator

Locations (1)

National Taiwan University Hospital

Taipei, Taiwan, Taiwan

Key Dates

Start Date

June 1, 2014

Primary Completion Date

December 1, 2015

Completion Date

June 1, 2016

Last Updated

April 1, 2015

Enrollment

ESTIMATED participants

Conditions

Pompe Disease

Interventions

continuous positive airway pressure

PROCEDURE

Contacts

Yin-Hsiu Chien

CONTACT

886223123456 chienyh@ntu.edu.tw

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Data Source & Attribution

This clinical trial information is sourced from ClinicalTrials.gov, a service of the U.S. National Institutes of Health.

ClinicalTrials.gov last update: April 1, 2015Data synced to Clareo: March 29, 2026

Modifications: This data has been reformatted for display purposes. Eligibility criteria have been parsed into inclusion/exclusion sections. Location data has been geocoded to enable distance-based search. For the authoritative and most current information, please visit ClinicalTrials.gov.

Neither the United States Government nor Clareo Health make any warranties regarding the data. Check ClinicalTrials.gov frequently for updates.

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CPAP for Infantile Pompe Disease

Inclusion Criteria

Exclusion Criteria

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